This study is in progress, not accepting new patients
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease
Summary
- Eligibility
- for people ages 18 years and up (full criteria)
- Location
- at Los Angeles 5368361, California 5332921 and other locations
- Dates
- study startedstudy ends around
- Principal Investigator
- by Jeff M. Bronstein, MD, PhD

Description
Summary
Official Title
Details
Keywords
Eligibility
Locations
Lead Scientist at UCLA
- Jeff M. Bronstein, MD, PhD
Jeff Bronstein, M.D., Ph.D., holds the Fred Silton Family Chair in Movement Disorders.
Details
- Status
- in progress, not accepting new patients
- Start Date
- Completion Date
- (estimated)
- Sponsor
- Ultragenyx Pharmaceutical Inc
- Links
- Ultragenyx Patient Advocacy/Wilson Disease Information Ultragenyx Wilson Disease (WD) Research Study Opportunities Ultragenyx Transparency Commitment Sign up for this study
- ID
- NCT04884815
- Phase
- Phase 1/2 Wilson's Disease Research Study
- Study Type
- Interventional
- Participants
- Expecting 82 study participants
- Last Updated