Muscular Dystrophies clinical trials at UCLA
3 in progress, 0 open to eligible people
AOC 1020 in Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)
Sorry, accepting new patients by invitation only
A Phase 2 Open-label Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of AOC 1020 Administered Intravenously to Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)
Los Angeles, California and other locations
AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)
Sorry, in progress, not accepting new patients
A Randomized, Double-blind, Placebo-controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory Efficacy of AOC 1020 Administered Intravenously to Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)
Los Angeles, California and other locations
SAT-3247 in Pediatric Ambulatory Patients
Sorry, in progress, not accepting new patients
Phase 2a trial of SAT-3247 in ambulatory DMD patients aged ≥ 7 and < 10 years. The trial will study two doses of SAT-3247 in a randomized, double-blind, placebo-controlled weekday regimen for 12 weeks to determine the optimal dose, safety, tolerability, and preliminary efficacy.
Los Angeles, California and other locations
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