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Myotonic Disorders clinical trials at UCLA

2 in progress, 0 open to eligible people

Showing trials for
  • Global Open-Label Extension Study of Del-desiran for the Treatment of DM1

    Sorry, accepting new patients by invitation only

    A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous Delpacibart Etedesiran (abbreviated del-desiran, formerly AOC 1001) for the Treatment of Myotonic Dystrophy Type 1

    Los Angeles 5368361, California 5332921 and other locations

  • Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients

    Sorry, in progress, not accepting new patients

    AOC 1001-CS2 (MARINA-OLE) is a Phase 2 extension of the AOC 1001-CS1 (MARINA) study to evaluate the safety, tolerability, efficacy, pharmacokinetics and pharmacodynamics of multiple-doses of AOC 1001 Administered Intravenously to Adult Myotonic Dystrophy Type 1 (DM1) patients

    Los Angeles 5368361, California 5332921 and other locations

Our lead scientists for Myotonic Disorders research studies include .

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