This study is in progress, not accepting new patients
Microdystrophin Gene Transfer Study in Adolescents and Children With DMD
Summary
- Eligibility
- for males ages 4-17 (full criteria)
- Location
- at Los Angeles, California and other locations
- Dates
- study startedcompletion around
- Principal Investigator
- by Perry Shieh
Description
Summary
Official Title
Keywords
Eligibility
Locations
Lead Scientist at UCLA
- Perry Shieh
HS Clinical Professor, Neurology, Medicine. Authored (or co-authored) 88 research publications
Details
- Status
- in progress, not accepting new patients
- Start Date
- Completion Date
- (estimated)
- Sponsor
- Solid Biosciences Inc.
- ID
- NCT03368742
- Phase
- Phase 1/2 Duchenne Muscular Dystrophy Research Study
- Study Type
- Interventional
- Participants
- About 12 people participating
- Last Updated