Mucopolysaccharidosis clinical trials at UCLA

3 in progress, 1 open to eligible people

Showing trials for

  • ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II)

    open to eligible males ages up to 6 years

    The main aim of this study is to evaluate the ability of a prophylactic immune tolerizing regimen (ITR) to prevent or reduce the development of high titer anti-idursulfase antibodies in treatment-naïve participants with Hunter syndrome. In this open …

    Torrance, California and other locations

  • Cannabidiol in Sanfilippo Syndrome

    Sorry, not yet accepting patients

    The goal of this clinical trial is to test cannabidiol in Sanfilippo syndrome. The main questions it aims to answer are: 1) determine the safety of cannabidiol in Sanfilippo syndrome, and 2) explore the efficacy of cannabidiol in treating the…

    Torrance, California

  • Adalimumab in MPS I, II, and VI

    Sorry, in progress, not accepting new patients

    Randomized, double-blind, placebo-controlled, parallel-group, single-center study followed by open-label phase, to evaluate the effects of adalimumab compared to placebo on the change from baseline in joint and skeletal disease in children and…

    Torrance, California

Our lead scientists for Mucopolysaccharidosis research studies include .

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