Angelman Syndrome clinical trials at UCLA
2 in progress, 0 open to eligible people
Showing trials for
Long-term Extension of GTX-102 in Angelman Syndrome
Sorry, in progress, not accepting new patients
The primary objective of the study is to evaluate the long-term safety profile of GTX-102 in participants with Angelman Syndrome (AS)
Los Angeles, California and other locations
REVEAL: A Phase 3 Study of Obudanersen (ION582) in Angelman Syndrome
Sorry, in progress, not accepting new patients
The purpose of this study is to evaluate the efficacy and safety of obudanersen in children and adults with Angelman syndrome caused by a deletion or mutation of the UBE3A gene.
Los Angeles, California and other locations
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